Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in BTK/Tec double deficient X-linked agammaglobulinemia model › Research Explorer

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Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in BTK/Tec double deficient X-linked agammaglobulinemia model

Research output: Contribution to journal › Article › peer-review

DOI

https://doi.org/10.1039/d4cb00312h
Final published version

Burcu Bestas
H. Yesid Estupiñán
Qing Wang
Shabnam Kharazi
Chenfei He
Dara K. Mohammad
Dhanu Gupta
Oscar P.B. Wiklander
Taavi Lehto
Karin E. Lundin
Anna Berglöf
Mikael C.I. Karlsson
Frank Abendroth
Samir El Andaloussi
Michael J. Gait
Matthew J.A. Wood
Christian J. Leumann
Robert Månsson
Jesper Wengel
Rula Zain
C. I.Edvard Smith

Original language	English
Pages (from-to)	761-771
Number of pages	11
Journal	RSC Chemical Biology
Volume	6
Issue number	5
Early online date	31 Mar 2025
DOIs	https://doi.org/10.1039/d4cb00312h
Publication status	Published - 8 May 2025

OECD FOS+WOS

ID: 65194774