Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in BTK/Tec double deficient X-linked agammaglobulinemia model

Bestas, B., Estupiñán, H. Y., Wang, Q., Kharazi, S., He, C., K. Mohammad, D., Gupta, D., Wiklander, O. P. B., Lehto, T., Lundin, K. E., Berglöf, A., Karlsson, M. C. I., Abendroth, F., El Andaloussi, S., Gait, M. J., Wood, M. J. A., Leumann, C. J., Stetsenko, D. A., Månsson, R., Wengel, J., & 2 othersZain, R. & Smith, C. I. E., 8 May 2025, In: RSC Chemical Biology. 6, 5, p. 761-771 11 p.

Research output: Contribution to journal › Article › peer-review

Key thermodynamic characteristics of Cas9 and Cas12a endonucleases’ cleavage of a DNA substrate containing a nucleotide mismatch in the region complementary to RNA

Baranova, S. V., Zhdanova, P. V., Pestryakov, P. E., Chernonosov, A. A. & Koval, V. V., 1 Jul 2025, In: Biochemical and Biophysical Research Communications. 768, p. 151892 151892.

Research output: Contribution to journal › Article › peer-review